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Tarix Granted Orphan Drug Status For TXA127
2016-02-18 02:28:07| drugdiscoveryonline News Articles
Tarix Orphan LLC today announced that the U.S. Food and Drug Administration has granted Orphan Drug status to the company's lead compound, TXA127, for the treatment of laminin-deficient congenital muscular dystrophy (LAMA2 MD or MDC1A). Early-onset LAMA2-related muscular dystrophy occurs in approximately 1 in 30,000 individuals and accounts for between 30 and 40 percent of total cases of congenital muscular dystrophy.
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Category:Biotechnology and Pharmaceuticals