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03.04.16 -- Amarantus Requests Rare Pediatric Disease Designation From FDA

2016-03-03 00:19:04| drugdiscoveryonline Home Page

03/04/16 Drug Discovery Online Newsletter

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Amarantus Requests Rare Pediatric Disease Designation From FDA

2016-02-09 01:17:54| drugdiscoveryonline News Articles

Amarantus BioScience Holdings, Inc.(OTCQB: AMBS),a biotechnology company focused on developing products for Regenerative Medicine, Neurology and Orphan Diseases, announced that it has requested Rare Pediatric Disease Designation (RPDD) from the US Food and Drug Administration (FDA) for treating retinitis pigmentosa (RP) with MANF.

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New hope for rare 'stone man' disease, where flesh turns to bone

2015-09-02 23:41:08| Biotech - Topix.net

Researchers working with mice believe there's hope for patients with a rare genetic disorder that turns their muscle into bone, in essence immobilizing them in an extra skeleton. Called "stone man syndrome," this lethal disorder appears to be caused by mutations in a gene called ACVR1 that controls bone and muscle development, researchers report Sept.

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New hope for rare 'stone man' disease, where flesh turns to bone

2015-09-02 23:41:07| Biotech - Topix.net

Researchers working with mice believe there's hope for patients with a rare genetic disorder that turns their muscle into bone, in essence immobilizing them in an extra skeleton. Researchers working with mice believe there's hope for patients with a rare genetic disorder that turns their muscle into bone, in essence immobilizing them in an extra skeleton.

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Cambridge rare disease biotech Synageva to be acquired for $8.4B

2015-05-06 13:59:14| Biotech - Topix.net

Cambridge rare disease biotech Synageva BioPharma Corp. will be acquired for $8.4 billion by Connecticut-based Alexion Pharmaceuticals, the two companies announced today.

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