je.st
news
Tag: rare disease
03.04.16 -- Amarantus Requests Rare Pediatric Disease Designation From FDA
2016-03-03 00:19:04| drugdiscoveryonline Home Page
03/04/16 Drug Discovery Online Newsletter
Tags: disease
requests
rare
designation
Amarantus Requests Rare Pediatric Disease Designation From FDA
2016-02-09 01:17:54| drugdiscoveryonline News Articles
Amarantus BioScience Holdings, Inc.(OTCQB: AMBS),a biotechnology company focused on developing products for Regenerative Medicine, Neurology and Orphan Diseases, announced that it has requested Rare Pediatric Disease Designation (RPDD) from the US Food and Drug Administration (FDA) for treating retinitis pigmentosa (RP) with MANF.
Tags: disease
requests
rare
designation
New hope for rare 'stone man' disease, where flesh turns to bone
2015-09-02 23:41:08| Biotech - Topix.net
Researchers working with mice believe there's hope for patients with a rare genetic disorder that turns their muscle into bone, in essence immobilizing them in an extra skeleton. Called "stone man syndrome," this lethal disorder appears to be caused by mutations in a gene called ACVR1 that controls bone and muscle development, researchers report Sept.
New hope for rare 'stone man' disease, where flesh turns to bone
2015-09-02 23:41:07| Biotech - Topix.net
Researchers working with mice believe there's hope for patients with a rare genetic disorder that turns their muscle into bone, in essence immobilizing them in an extra skeleton. Researchers working with mice believe there's hope for patients with a rare genetic disorder that turns their muscle into bone, in essence immobilizing them in an extra skeleton.
Cambridge rare disease biotech Synageva to be acquired for $8.4B
2015-05-06 13:59:14| Biotech - Topix.net
Cambridge rare disease biotech Synageva BioPharma Corp. will be acquired for $8.4 billion by Connecticut-based Alexion Pharmaceuticals, the two companies announced today.
Tags: disease
rare
acquired
cambridge