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Tag: rare disease
2-year-old battles rare disease
2014-03-08 07:49:24| Industrial Machines - Topix.net
An Omaha boy is one of only 2,000 in the world with a rare disorder called Hunter syndrome, and with little research available, his family is leading the charge to find out what might stop it.
Tags: disease
rare
battles
rare disease
NIH Scientists Pursue New Therapies To Improve Rare Disease Drug Development
2013-10-02 06:18:51| drugdiscoveryonline News Articles
Four new pre-clinical drug development projects at the National Institutes of Health will target a form of blindness and diseases characterized by cardiac problems. The projects were selected for their potential to treat specific rare diseases and to help scientists uncover new information that can be shared with other researchers
Tags: development
improve
drug
disease
MassBio panel tackles why rare disease treatments cost so much
2013-03-17 19:52:04| Biotech - Topix.net
David Meeker, right, CEO of Genzyme Corp., speaks at a panel on pricing of rare disease therapies at the MassBio annual meeting.